Preliminary Conference Program

May 22-23, Phoenix, Arizona, US

3rd International GBA1 Meeting 2026

Satellite meeting of World Parkinson’s Congress

8:00

9:00

Registration & Breakfast

9:00

9:10

Topics

Welcome and opening remarks

Speaker

Ziv Gan-Or

9:10

9:40

Topics

Keynote presentation

Recent developments in GBA1 research and treatment

Speaker

-

9:40

10:30

9:40 – 10:00

10:00 – 10:20

10:20 – 10:30

Session

GBA1 therapeutics

Overview of GBA1-targeting trials

Report on the ACTIVATE trial

Q&A

Speaker

-

-

-

-

30 mins

Coffee Break

11:00

12:30

11:00 – 11:20

11:20 – 11:40

11:40 – 12:00

12:00 – 12:20

12:20 – 12:30

Topics

Advances in GBA1 mechanisms

Bidirectional regulation of GPNMB by β-glucocerebrosidase deficiency

The Cholinergic system in GBA1-PD

Targeting Lysosomal pH Restores Mitochondrial Quality Control in GBA1-Mutant Parkinson's Disease

Lysosomal glucocerebrosidase is needed for ciliary Hedgehog signaling

Q&A

Speaker

-

-

-

-

-

-

12:30

14:30

Lunch + Poster session 

14:30

15:30

14:30 – 14:40

14:40 – 14:50

14:50 – 15:00

15:00 – 15:10

15:10 – 15:20

15:20 – 15:30

Topics

Data Blitz 1 (selected from abstracts)

TBD

TBD

TBD

TBD

TBD

TBD

Speaker

-

TBD

TBD

TBD

TBD

TBD

TBD

30 mins

Coffee Break

16:00

17:00

16:00 – 16:15

16:15 – 16:30

16:30 – 16:45

16:45 – 17:00

Topics

In the pipeline: updates from pharma on ongoing preclinical studies and clinical trials

Update from company A

Update from company B

Update from company C

Q&A

Speaker

Chair: Ziv Gan-Or

Company A

Company B

Company C

-

18:00

21:00

Cocktail Reception + meet the experts

8:00

9:00

Registration & Breakfast

9:00

9:10

Topics

Announcement of trainee awards for best poster /oral presentation

Speaker

Ziv Gan-Or

9:10

10:10

9:10 – 9:40

9:40 – 10:00

10:00 – 10:10

Session

Novel therapeutic approaches for GBA1-associated diseases

Keynote presentation - Can gene editing become the future for GBA1-associated diseases?

Lipid nanoparticles for brain delivery

Q&A

Speaker

-

-

-

-

30 mins

Coffee Break

10:40

12:00

10:40 – 10:50

10:50 – 11:00

11:00 – 11:10

11:10 – 11:20

11:20 – 11:30

11:30 – 11:40

11:40 – 11:50

11:50 – 12:00

Topics

Data Blitz 2

TBD

TBD

TBD

TBD

TBD

TBD

TBD

TBD

Speaker

-

TBD

TBD

TBD

TBD

TBD

TBD

TBD

TBD

12:00

14:00

Lunch + Poster session 

14:00

15:30

14:00 – 14:20

14:20 – 14:40

14:40 – 15:00

15:00 – 15:20

15:20 – 15:30

Topics

Clinical considerations in GBA1-PD

The global burden of GBA1-PD

GBA1 variant classification for clinical trials

Advances in biomarkers for GBA1 clinical research

Treatment of non-motor symptoms in GBA1-PD

Q&A

Speaker

-

-

-

-

-

-

30 mins

Coffee Break

16:00

17:00

16:00 – 16:20

16:20 – 16:40

16:40 – 17:00

Topics

GBA1 modifiers and clinical implications

Interplay between ATP13A2, glucocerebrosidase and BMP

Structural insights into the activation of TMEM175 by small molecule

Concluding remarks

Speaker

-

-

-

-

18:00

20:00

Event for people with PD – dinner + general public talk